26.49 Randomized controlled trial

  • By far the most important experimental study is the Randomized Controlled Trial
  • A single variable is randomly assigned; this may be called the independent variable and is usually a treatment.
  • Each different treatment is called an arm of the study. The outcome variables are clinical, radiographic, or functional measures of the success of management
  • Randomization limits the dependence of outcome variables on other factors in the study (e.g., gender, age, fracture severity), thus helping to isolate the effect of the treatment on outcomes

  • These other factors are often called confounding variables, because they may also influence the outcome variables if they are not properly addressed
  • Randomized control trials control for confounding and bias and isolate the effect of the treatment on the outcomes (to the greatest extent possible)
  • The disadvantages are cost, complexity, and the ethical considerations involved in randomly assigning treatments

  • Several modifications of Randomized control trials are important.
    • Crossover studies – These involve switching patients between different arms of the study.
      • For example, one arm may receive physical therapy for 4 weeks and another arm medical therapy for 4 weeks. Then the patients switch therapies for another 4 weeks.
      • Such patients may act as their own controls and increase the power of the study.
      • If patients wait a period of time between therapies, receiving no therapy, this is a washout period in which the effect of the first therapy is allowed to wear off.
    • Partial compliance – Many Randomized control trials involve imperfect compliance with the study protocol by patients who find the protocol difficult to adhere to
      • If this effect is large, special analytic methods are needed to increase confidence in the results